Having recently submitted govorestat on both sides of the Atlantic for galactosemia, Applied Therapeutics Inc. will be knocking on the regulators' doors again soon on the back of more impressive data, this time evaluating the drug for sorbitol dehydrogenase (SORD) deficiency.
Applied Therapeutics Takes Strong Swipe At SORD With Govorestat
Govorestat could soon be filed for a second indication after impressing as a potential treatment for SORD deficiency, one of the most common forms of recessive hereditary neuropathy for which there are no approved therapies.
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