With its first drug approval and the first approved therapy for the ultra-rare immunodeficiency disorder WHIM syndrome, X4 Pharmaceuticals, Inc. told a 29 April investor call that while Xolremdi (mavorixafor) will be available immediately, it sees 2024 as a year for laying the groundwork for clinician understanding and payer acceptance of the drug.
Key Takeaways
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About two years after a 20% staff cut, X4 gets its first FDA approval for Xolremdi in the rare immunodeficiency disorder WHIM syndrome.
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The biotech sets pricing at $372,000-$496,000 per year and says early launch months will focus on setting up the market
Xolremdi is a once-daily capsule indicated in the US as a 400mg dose in patients weighing more than 50kg and dosed at 300mg in patients at or below 50kg. It will carry a wholesale acquisition cost of $496,000 for the higher dose and $372,000 for the lower dose
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