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NGGT Progresses First US Gene Therapy Trials For Rare Conditions

Supported By China Data

 
• By Dexter Jie Yan

Next Generation Gene Therapeutics is fast-tracking clinical trials in the US for its gene therapy candidates for Bietti's crystalline dystrophy and classic phenylketonuria, supported by China data, the Chinese venture's CEO tells Scrip in an interview.

US China flags
NGGT leveraging China's large rare disorder patient pools to speed up US trials • Source: Shutterstock

For global developers of rare disease drugs, China and its 1.4 billion population may offer relatively large pools of patients with such disorders. Clinical data derived from trials in the country can also be used to help speed up clinical studies in the US or Europe.

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