With the number of US Food and Drug Administration-approved gene therapies set to balloon from fewer than 20 to about 100 by the early 2030s, the challenges of paying for them are bound to balloon as well, with total list-price spending potentially equivalent to the gross domestic products of some small countries. A recent report on the reimbursement models for gene therapies by the Institute for Clinical and Economic Review (ICER) and Tufts Medical Center’s NEWDIGS looks at the potential to combine strategies like reinsurance and rebates.
Could Combining Strategies Be A Way Forward To Pay For Gene Therapies?
A report by ICER and Tufts Medical Center’s NEWDIGS said a single strategy cannot adequately address payment challenges for all payers.

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The promise of innovative therapies seems to have been constrained not by efficacy or safety concerns, but because the high price of treatments is incongruous with the reimbursement of short-course therapies.
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Encouraging results in younger children with Duchenne is keeping Regenxbio on track for a potential mid-2026 filing for its gene therapy, RGX-202.
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Amgen’s AI model to predict proteins in the “bright Goldilocks zone of viscosity” with over 80% accuracy minus a wet lab experiment holds immense potential, VP Research Haldar said at an event as he spoke about a “hinge moment” for AI in pharma