The status quo for patients with serious diseases is often death, disability, or poor quality of life. What if I told you that status quo is changing? Ten years ago, Emily Whitehead had run out of treatment options for her leukemia. As a last resort, Emily’s parents agreed to an experimental cell therapy never tested in children. Now, 10 years later, Emily is considered cured by this CAR-T therapy.
The Cell And Gene Therapy Sector In 2023: A Wave Is Coming – Are We Ready?
From a scientific perspective, the outlook for patient with rare disease has never been brighter. This year, 13 new cell or gene therapies could be approved in the US, Europe or both by the end of 2023. However, the challenges that stop patients accessing new therapies remain. Could this year be the turning point when our health care systems start to catch up with our science?
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