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BioMarin impresses with Phase II dwarfism drug

 
• By Lucie Ellis-Taitt

BioMarin Pharmaceuticals has raised expectations for its dwarfism product BMN-111 (vosoritide) on the back of strong Phase II data.

BioMarin Pharmaceuticals has raised expectations for its dwarfism product BMN-111 (vosoritide) on the back of strong Phase II data.

In the study in 26 children, BMN-111 demonstrated a favorable safety profile and efficacy at the 15µg/kg daily dose. The 10 children in Cohort 3 treated with 15 µg/kg/day had...

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