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Modus CEO Says Rare Disease Priority Review Voucher To Be Key Catalyst

 
• By Sten Stovall

The US FDA gives Sweden's privately held Modus Therapeutics rare pediatric disease designation for sickle cell disease.

Sickle cells
Sevuparin is an anti-adhesive drug now in Phase II Trials in "core" SCD countries • Source: Shutterstock

In a key catalyst for the small biotech, Modus Therapeutics AB has won rare pediatric disease designation from the FDA, raising the Swedish group's chances of winning a coveted rare disease priority review voucher if it wins marketing approval for its sickle cell disease candidate therapy sevuparin.

Sevuparin, currently in Phase II trials in "core" sickle cell countries bordering Africa, is a modified low-molecular weight heparin which has no anti-coagulant effect anymore but is able to prevent...

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