Capricor’s Interim Data Could Offer Hope For Older DMD Patients

Although only interim data from six treated patients, Capricor’s Phase II DMD study shows improvements in upper limb performance, grip strength and respiration. Cardiac performance shows positive trend, but not yet statistical significance.

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Capricor's interim data may offer hope to older DMD patients

In a disease with limited therapies for patient subgroups and a landscape littered with clinical setbacks, Capricor Therapeutics Inc.’s interim Phase II data indicate that its intravenous cell therapy can yield statistically significant improvements in upper limb strength and function, grip strength and respiratory function in older Duchenne muscular dystrophy (DMD) patients who lack treatment options.

Before the markets opened on 15 July, the Los Angeles-based firm revealed that CAP-1002 showed statistical significance in the Phase...

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