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Sickle Cell Disease Market Snapshot: "The Time Has Come"

 
• By Jessica Merrill

Three new drugs for sickle cell disease could be on the market in the US next year, representing a groundswell of advancement for the devastating blood disorder that has had limited options.

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Big changes are in store for the sickle cell disease treatment market • Source: Shutterstock

With one new drug on the market in the US and two more pending at the US Food and Drug Administration, 2020 is positioned to be a turning point for the treatment of sickle cell disease. Patients with the devastating blood disorder, which results in acute pain crises, long-term organ damage and a shortened lifespan, have had few treatment options, but the outlook for sickle cell R&D is brighter than it has been.

"The time has come. We are at the cusp of improving the quality of life for people with sickle cell...

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