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Intellia To Take On Pfizer Blockbuster With Gene-Editing Therapy

Aims To Challenge Vyndaqel

 
• By Andrew McConaghie

After achieving a landmark in gene-editing with NTLA-2001, Intellia moves to expand its reach into a larger market.

Intellia HQ
It is still early days for its vivo gene-editing therapy NTLA-2001, but Intellia is accelerating its challenge Pfizer. • Source: Alamy

Intellia Therapeutics, Inc. has broadened a trial of its in vivo gene-editing candidate NTLA-2001 in order to take on Pfizer’s rare disease blockbusters Vyndaqel and Vyndamax.

The genome-editing company achieved a landmark last June with partner Regeneron Pharmaceuticals when they unveiled the first results from NTLA-2001, a CRISPR-Cas9 gene-editing therapy which works directly in the...

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