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Sanofi Posts More Positive Olipudase Alfa Data As Approval Decisions Loom

First Potential Therapy For Rare Lysosomal Storage Disease

 
• By Kevin Grogan

Ahead of a PDUFA date of 3 July, Sanofi has added to the body of clinical evidence supporting olipudase alfa as a treatment for acid sphingomyelinase deficiency (ASMD), a rare, progressive and potentially life-threatening disease with no approved therapies.

Paperwork
Sanofi amasses more data on olipudase alfa • Source: Alamy

As it awaits approvals on both sides of the Atlantic and in Japan for olipudase alfa, Sanofi has trumpeted more positive data on what could soon be the first therapy for acid sphingomyelinase deficiency (ASMD), a rare lysosomal storage disease.

The French major has presented results at the lyso

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