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ITF Has A Fight On Its Hands In Duchenne

 
• By Elizabeth Cairns

The group’s new muscular dystrophy pill seems unlikely to cut into Sarepta’s sales.  

Box fighters trainning outdoor . Mixed media

The sellside sees the Duchenne muscular dystrophy market as pretty much sewn up by Sarepta Therapeutics, Inc.. That group had the top three products on the market last year, and its new gene therapy, Elevidys (delandistrogene moxeparvovec), has 2028 sales forecasts of more than $3bn, Evaluate Pharma data show.

Key Takeaways
  • ITF Therapeutics’ Duchenne muscular dystrophy therapy Duvyzat has been given a broad label
  • But Sarepta dominates the space, with expectations for its gene therapy Elevidys particularly high
  • ITF may have to

Last week, though, a new player entered the game: Italfarmaco S.p.A., via its purpose-built US subsidiary, ITF Therapeutics. On 22 March, the US Food and Drug Administration approved ITF’s Duvyzat (givinostat), the first oral, non-steroidal drug for Duchenne

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