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Ascendis’ TransCon Positioned To Take On BioMarin’s Voxzogo

 
• By Jessica Merrill

The Danish company released pivotal data for TransCon CNP in children with achondroplasia that appears competitive with BioMarin’s big growth driver.

Ascendis announced positive Phase III data that hit the mark with investors • Source: Shutterstock

Ascendis Pharma A/S is preparing to file a new drug application for TransCon CNP (navepegritide) early next year for treatment of the growth condition achondroplasia after announcing positive results from the Phase III ApproaCH trial on 16 September.

TransCon CNP is intended to rival to BioMarin Pharmaceutical Inc.’s Voxzogo (vosoritide), which was granted accelerated approval by the...

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