US FDA's Record-Breaking Month Of Breakthrough Therapy Designations

Alnylam's ALN-AS1 became the eighth announced therapy to receive a breakthrough designation in May 2017, breaking the previously monthly high of seven.

Alnylam Pharmaceuticals has capped off a busy month of breakthrough therapy recipients, with the company announcing the designation May 31 for its ALN-AS1 (givosiran) an RNAi treatment designed for the prevention of attacks in patients with acute hepatic porphyria.

A family of rare diseases, acute hepatic porphyrias can result in patients experiencing severe neurovisceral attacks that can lead to...

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