FDA’s Peter Stein On Hitting The ‘Persuasive Evidence’ Bar For Rare Disease Drug Repurposing

14 Feb 2023

The Office of New Drugs head discussed the types of data the agency might be willing to accept to repurpose a drug for a rare disease and laid out three ways to search for other uses of approved medicines.

old bicycle used as planter — The regulatory pathway can be simpler for repurposed drugs, the FDA’s Peter Stein said. • Source: Shutterstock

FDA’s Peter Stein On Hitting The ‘Persuasive Evidence’ Bar For Rare Disease Drug Repurposing

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