Pediatric And Rare Disease Drug Development Legislation Clears US House Committee

As amended, the Give Kids A Chance Act would renew the rare pediatric disease voucher program for five years and give the FDA new authority to bring enforcement action when pediatric studies are overdue. However, it would not remove the exemption from pediatric study requirements for non-cancer orphan drugs, which Democrats had sought. 

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A bipartisan package of measures targeting rare and pediatric disease drug development cleared a House committee. • Source: Shutterstock

Legislation to spur development of treatments for pediatric and rare diseases easily cleared a US House committee on 18 September, boosting chances for inclusion in an end-of-year omnibus package.

An amended version of the Give Kids A Chance Act of 2024 (H.R. 3433) advanced out of the House...

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