England’s health technology assessment (HTA) agency, NICE, has formally agreed to reimburse Vertex/CRISPR Therapeutics AG’s CRISPR/Cas9-based gene editing therapy Casgevy (exagamglogene autotemcel), also known as exa-cel, to treat patients with sickle cell disease (SCD).
Gene Editing Therapy Casgevy Now Funded In 8 Countries But French Access Withdrawn
The world’s first CRISPR gene editing therapy, Casgevy, has been made available to patients with sickle cell disease in England, adding to access arrangements in the US, Austria, Bahrain, Germany, Luxembourg, Italy and Saudi Arabia.
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