For Rare and Rapidly Progressing Disease US FDA Has Heard ‘Well and Clear’ Placebo Is Unacceptable

 
• By Sarah Karlin-Smith
  
one single human arm raised up on an angle
The FDA's Lola Fashoyin-Aje said the agency understands people do not want to enroll in randomized studies for rapidly progressing fatal diseases with no available therapies. (Shutterstock)

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