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EMA Says Yes To First Sickle Cell Drug For PRIME

 
• By Neena Brizmohun

Investigational drugs for sickle cell disease and diffuse large B cell lymphoma from Global Blood Therapeutics and Roche respectively have become the latest products to make it onto the European Medicines Agency’s PRIME scheme for speeding the development of drugs for unmet medical need.

Sickle cell anemia, 3D illustration showing blood vessel with normal and deformated crescent-like red blood cells
GBT hopes PRIME will speed development for its sickle cell disease drug

The European Medicines Agency has accepted the first investigational drug for treating sickle cell disease (SCD) onto its priority medicines (PRIME) program for getting products for unmet medical needs to patients faster.

GBT440 is being develop by Global Blood Therapeutics, which has met PRIME’s rigorous entry criteria and will now receive early...

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