6,000, 7,000, 10,000? Why Counting Rare Diseases Is So Difficult

 
• By Derrick Gingery

FDA, NIH, sponsors and others use different figures, but some want everyone will settle on 10,000 for policy discussions, advocacy and research.

consensus
Advocates also want to verify the number of US patients with a rare disease and the number of rare diseases with pediatric onset. • Source: Shutterstock

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