Elevidys Payer Gauntlet Complicated By Fear Patients Could Age Out Of DMD Gene Therapy’s Label

Launching much faster than it told a US FDA advisory committee that it would, Sarepta is focusing on Duchenne muscular dystrophy patients about to turn six in the initial roll-out of its gene therapy Elevidys amid fears the wait for payer authorization could mean losing access to the treatment.

Hourglass
Many DMD patients are hoping time does not run out on their access to Elevidys. • Source: Shutterstock

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