Rare diseases are finally getting their due in the US Food and Drug Administration’s advisory committee system.
On 12 December, the FDA announced the establishment of a new expert panel – the Genetic Metabolic Diseases Advisory Committee...
In a first for rare diseases, a new standing committee will provide advice and recommendations on technical, scientific and policy issues related to medical products for genetic metabolic diseases.
Rare diseases are finally getting their due in the US Food and Drug Administration’s advisory committee system.
On 12 December, the FDA announced the establishment of a new expert panel – the Genetic Metabolic Diseases Advisory Committee...