Rare diseases are finally getting their due in the US Food and Drug Administration’s advisory committee system.
On 12 December, the FDA announced the establishment of a new expert panel – the Genetic Metabolic Diseases Advisory Committee...
Genetic Metabolic Diseases Get Their Own US FDA Advisory Committee
In a first for rare diseases, a new standing committee will provide advice and recommendations on technical, scientific and policy issues related to medical products for genetic metabolic diseases.
