Pharmaceutical companies have finally begun to use England’s £340m ($425m) Innovative Medicines Fund (IMF), more than a year after the scheme was first launched. Alexion’s Kanuma (sebelipase alfa) is the most recent of three drugs to be accepted for National Health Service funding via the IMF.
England’s Innovative Medicines Fund Picks Up Pace As Alexion’s Kanuma Gets Green Light
Alexion has secured funding for its Wolman disease drug Kanuma via England’s Innovative Medicines Fund after several years of “constructive collaboration” with the country’s health technology assessment body NICE and the National Health Service.

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Not all companies will be able to access joint scientific consultations under the EU Health Technology Assessment Regulation, but success is still possible for those that engage with national agencies early on, says EUCOPE’s Alexander Natz.
Payers and health technology assessment bodies in the Netherlands, Germany and Italy are either unwilling to use real-world data in assessments or cannot due to their existing frameworks, say representatives from Gilead Sciences and Autolus Therapeutics.
Companies have until 17 March to respond to an EU consultation on a new strategy that will seek to simplify the regulatory framework and make it easier for innovative small and medium-sized enterprises to “access the capital they need” to scale up in the bloc.
Center for Biologics Evaluation and Research Director Peter Marks expects no fundamental changes in support for FDA initiatives and said the Rare Disease Innovation Hub, which promotes cross-center collaboration, is “consistent with what we're hearing in the current environment.”
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South Korea announces planned revisions to a government scheme to designate "innovative" biopharma companies amid allegations of "discrimination" against foreign firms.