Hereditary Angioedema Patients Urge Work On Dosing, Product Shortages

US FDA's final patient-focused drug development meeting shows high interest clinical trial enrollment.

Hereditary angioedema patients used the final US FDA-hosted patient-focused drug development meeting to advocate for the development of additional treatment options for HAE, citing intermittent manufacturing supply issues with existing biologics and the lack of a treatment that sufficiently prevents or controls body swelling episodes.

HAE is a rare genetic disorder that is associated with painful episodic, recurrent attacks of body swelling caused by abnormalities...

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