Rare Pediatric Priority Review Voucher Program Seems Headed For Short-Term Renewal

 
• By Derrick Gingery

Chair of the House Energy and Commerce Committee raises questions about the priority review voucher program’s value, suggesting another limited extension may be upcoming.

Priority Review Voucher
An advocate for the PRV program said rare pediatric disease designations and approvals have increased since it launched.

Reauthorization of the rare pediatric disease priority review voucher program does not appear threatened by the House Energy and Commerce Committee, but the fact that questions about its value continue to emerge may be telling about its long-term future.

A 29 July legislative hearing on HR 4439, the Creating Hope Reauthorization Act, which would ensure the voucher opportunity...

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