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Zynteglo Funding Rejection Sets "Dangerous Precedent" For Gene Therapies In UK

Bluebird Bio Rails Against Negative Reimbursement Decision

 
• By Francesca Bruce

bluebird is "shocked and disappointed" at the draft negative reimbursement decision on Zynteglo in UK but measures outlined in the NICE methods review could change fortunes of gene and cell therapies if taken forward.

Gene editiing
NICE take on discounting is 'a threat to gene therapies' • Source: Shutterstock

UK health technology assessment body NICE has published draft guidance rejecting bluebird bio’s gene therapy Zynteglo for routine funding on the National Health Service. The decision making behind the guidance sends a negative signal to investors in gene therapies, warns the company.

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