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Ultra-Rare Tumors: Public-Private Partnership Eyed To Boost Drug Development

 
• By Sue Sutter

US FDA, Foundation for the NIH, and NCI are considering a new PPP aimed at creating a repeatable process for development of drugs to treat ultra-rare cancers where commercial viability is lacking. Stakeholders say industry incentives, IP issues and reimbursement need attention.

Open notebook
The envisioned public-private partnership would take a transparent, open-notebook approach to drug development for ultra-rare tumors. • Source: Shutterstock

The US Food and Drug Administration, along with government partners, is assessing the feasibility of establishing a public-private partnership focused on drug development for ultra-rare tumors.

The proposed initiative would be aimed at creating a repeatable process for end-to-end development of drugs to treat ultra-rare cancers where the unmet need is high but

Proposed Definition Of Ultra-Rare Tumors For The PPP

  • ~≤300 people in the US per year

  • Rare enough to be economically infeasible and not attractive for

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