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CSL Nabs First ‘Direct Access’ Funding Agreement In France For Its Gene Therapy

 
• By Eliza Slawther

CSL’s hemophilia B gene therapy Hemgenix is the first medicine to be granted reimbursement through France’s experimental “direct access” program, several months after England’s HTA body dubbed the one-time product too expensive for national funding.

3d rendered medical illustration of a sickle cell
• Source: Shutterstock

Hemgenix (etranacogene dezaparvovec), a one-time gene therapy from CSL Behring that has a US list price of $3.5m, has been granted full reimbursement for up to a year in France through a an exceptional access scheme launched two years ago.

France’s direct access program was introduced under a social security financing law that was passed in December 2021 (LFSS 2022). On 13 December, Hemgenix became the first medicine to receive...

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