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EMA Grants First Two PRIME Designations In 2024 To Ultragenyx & Sangamo

 
• By Neena Brizmohun

Ultragenyx’s antisense oligonucleotide for treating Angelman syndrome and Sangamo’s gene therapy for Fabry disease are the latest products to make it onto the European Medicines Agency’s priority medicines scheme.

The PRIME scheme aims to help developers of medicines for unmet medical needs • Source: Shutterstock

GTX-102, Ultragenyx Pharmaceutical’s drug candidate for treating Angelman syndrome, and isaralgagene civaparvovec, Sangamo Therapeutics’ investigational gene therapy for Fabry disease, have become the first two products to secure a place on the European Medicines Agency’s PRIME (priority medicines) scheme in 2024.

Both products were accepted onto the scheme for speeding up the development of medicines for unmet medical needs in

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