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RWD Key To Scottish Orkambi Deal

 
• By Francesca Bruce

Vertex has managed to secure a deal to provide Scottish cystic fibrosis patients with access to Orkambi and Symkevi. The promise of real world data and a price discount has convinced the Scottish government to say yes to the treatments, which had earlier been rejected by the Scottish Medicines Consortium.

Cystic fibrosis word cloud
Vertex Strikes Cystic Fibrosis Deal With Scottish Government • Source: Shutterstock

In a UK first, the Scottish authorities have changed their mind and agreed to fund Vertex’s cystic fibrosis drugs, Orkambi (lumacaftor/ivacaftor) and Symkevi (tezacaftor/ivacaftor). The company and the government have struck an agreement under which Vertex will offer a confidential discount and a commitment to gather real world data on use of the products.

Only last month, the health technology appraisal body, the Scottish Medicines Consortium, said Vertex had failed to justify the cost...

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